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CMS
Biomarker
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Becker muscular dystrophy
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Myotonic Dystrophy type 1
Treatment
Muscle
Errance diagnostique
Duchenne muscular dystrophy
Neuromuscular junction
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Glutamate
Amyotrophic lateral sclerosis
Heart failure
Rare diseases
Myotonic Dystrophy
Thymus
Long read sequencing
Thérapie génique
RNA biology
Exercise
Congenital myopathy
Male
Myotonic dystrophy type 1
Neuromuscular disease
MBNL
Brain
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COVID-19
Humans
Laminopathy
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Heart
Dystrophin
Regeneration
Transcriptomics
Myotonic dystrophy
Cancer
OPMD
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CRISPRi
Congenital muscular dystrophy
Autoimmune diseases
Muscular dystrophy
LMNA
Rare neuromuscular diseases
Satellite cells
Satellite cell
Dermatomyositis
Clinical trials
Trinucleotide repeat expansion
Lamin A/C
Antisense oligonucleotides
Lamin A/C LMNA gene
Animals
AAV
Inflammation
Aged
LMNA gene
Fabry disease
Cytoskeleton
Laminopathies
Fibrosis
Motoneuron
Cell therapy
DMD
PABPN1
Myopathy
Myoblasts
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Biomarkers
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Transgenic mouse model
Outcome measures
Alternative splicing
Diagnosis
Muscle regeneration
Nuclear envelope
ALS
Dynamin 2
Mechanotransduction
Mouse model
Myositis
CTG repeat contractions
Neuromuscular diseases
Genotype phenotype correlation